NEAXUSINSTITUTE OF BIODISCOVERY
Research Hub

Computational Biology & Genomic Initiatives

Documentation for active research projects, simulation studies, and variant reasoning models. All project output includes explicit evidence classification.

★ Flagship InitiativeSTATUS: ExploringEVIDENCE // Preliminary
System: Lysosomal Membrane & Endosomal Cholesterol Export Pathway

NPC1 Cholesterol Transport Dynamics & Lysosomal Trafficking

Computational modeling of sterol sensing domain mutations in Niemann-Pick disease type C1.

Niemann-Pick C1 (NPC1) is a 13-pass transmembrane lysosomal membrane protein essential for intracellular cholesterol export. Mutations in NPC1 lead to lysosomal lipid accumulation and progressive neurodegeneration. This project investigates variant-level conformational shifts using molecular dynamics simulations and machine learning residue contact graphs.

CORE RESEARCH QUESTION

How do missense variants in the sterol-sensing domain alter cholesterol transfer kinetics between NPC2 and NPC1?

STATUS: ModelingEVIDENCE // Hypothesis
System: Human Genome-Wide Exome & Metabolic Pathways

Variant-Level Biological Reasoning & Annotation Engine

Combining evolutionary protein embeddings with metabolic network topologies for rare disease variant scoring.

Standard variant effect predictors rely heavily on sequence conservation. This initiative integrates tissue-specific gene expression networks and protein structural dynamics to improve biological interpretability for unclassified variants (VUS).

CORE RESEARCH QUESTION

Can structural contact graph features resolve ambiguous VUS designations in lysosomal storage disorder genes?

STATUS: LearningEVIDENCE // Simulation
System: Endo-Lysosomal System & Autophagy Axis

Computational Pathway Flux & Organelle Homeostasis

Systems-level dynamic ODE modeling of lysosomal lipid recycling.

Simulating whole-organelle lipid fluxes to determine how disruption in single transporters cascades into cellular stress responses, autophagy inhibition, and mitochondrial dysfunction.

CORE RESEARCH QUESTION

At what critical threshold of cholesterol accumulation does lysosomal membrane permeabilization trigger cell death pathways?

LAMP1LAMP2TFEBMTOR